Evaluating Efficiencies of Dual AAV Approaches for Retinal Targeting
نویسندگان
چکیده
منابع مشابه
Evaluating Efficiencies of Dual AAV Approaches for Retinal Targeting
Retinal gene therapy has come a long way in the last few decades and the development and improvement of new gene delivery technologies has been exponential. The recent promising results from the first clinical trials for inherited retinal degeneration due to mutations in RPE65 have provided a major breakthrough in the field and have helped cement the use of recombinant adeno-associated viruses ...
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ژورنال
عنوان ژورنال: Frontiers in Neuroscience
سال: 2017
ISSN: 1662-453X
DOI: 10.3389/fnins.2017.00503